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2017
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A call for European projects on innovative therapeutic approaches for rare diseases

This call for proposals is now closed. You can view all open calls for proposals by clicking here.

The French National Research Agency will launch, in partnership with 16 countries, the ninth E-Rare joint call for funding multilateral research projects on rare diseases on “Innovative therapeutic approaches for rare diseases”.

The aim of the call is to enable scientists in different countries to build an effective collaboration on a common interdisciplinary research project based on complementarities and sharing of expertise, with a clear translational research approach. Projects shall involve a group of rare diseases or a single rare disease following the European definition i.e. a disease affecting not more than five in 10.000 persons in the European Community, EC associated states and Canada.

Towards innovative therapeutic approaches

The specific objective of this call is to promote research projects focusing on the pre-clinical development of therapeutic approaches in suitable existing animal or cell models.

Therapeutic approaches can include:

  • Cell-based therapy (e.g. somatic cell therapy, cell-based regenerative medicine, tissue engineering, therapies based on combination of cells with scaffolds or substrates, etc.);
  • Gene therapy (e.g. transfer of nucleic acids for therapeutic purposes including DNA, RNA, oligonucleotides, etc.);
  • Pharmacological therapy (e.g. use of chemicals or biopharmaceuticals including repurposing approaches, high throughput screening of molecules, etc.).

The research projects submitted within this call must be based on novel ideas stemming from consolidated previous results and must be clearly endowed with a strong translational research orientation, i.e. bench to bed studies allowing a rapid implementation into public health-related decisions or into the clinics.

The use of existing European health research infrastructures or initiatives is strongly encouraged when appropriate. The following European Research Infrastructures or Initiatives were identified as potentially useful for this kind of study: BBMRI; EATRIS; ECRIN; ELIXIR; EU-OPENSCREEN; INFRAFRONTIER; RD-Connect and European Medicines Agency.

Submission and evaluation of projects will be carried out in two stages and integrated with other countries. Each country shall fund its national teams according to its own procedures.

The deadline for proposal pre-registration is February 1st, 2017.
The deadline for proposal submission is June 2nd, 2017.

 

ARE EXCLUDED FROM THIS CALL FOR PROPOSALS: (1) therapeutic approaches concerning rare infectious diseases, rare cancers and rare adverse drug events in treatments of common diseases; (2) Interventional clinical trials or any project enrolling patients; (3) Development of new cell or animal models. The relevant cell or animal model must be already established for the purpose of the project; (4) Surgery or radiation therapies.

General information

The specific annex for French partners is available on this site. The call text, proposal templates, and guidelines for applicants are available on this site or on www.e-rare.eu.
Research project consortia who intend to submit a transnational proposal should register as soon as possible at https://www.pt-it.de/ptoutline/ERARE17. Electronic proposal submission is mandatory on: https://www.pt-it.de/ptoutline/ERARE17
No proposal submissions will be accepted directly at ANR.

Contact person for the Joint Call Secretariat:
Ms Maria Druet
mdruet@nullisciii.es ; (+34) 91 822 2530

ANR Contacts :
Dr. Juliane HALFTERMEYER:
E-RareCalls@nullagencerecherche.fr ; +33 (0)1 78 09 80 22
Dr. Daria JULKOWSKA:
E-RareCalls@nullagencerecherche.fr ; +33 (0)1 78 09 80 78

Release date of the call: Monday 5 December 2016

Deadline for submission of pre-proposals: Wednesday 1 February 2017 17:00

Deadline for submission of proposals: Friday 2 June 2017 17:00